FDA Approves Novel Gene Therapy for Spinal Muscular Atrophy in Newborns: 95% Success in Preventing Severe Symptoms
FDA fast-tracks gene therapy for spinal muscular atrophy in newborns, boasting 95%…
FDA Approves Revolutionary Gene Therapy for Rare Neuromuscular Disease, Achieving 80% Efficacy in Halting Progression
FDA fast-tracks gene therapy for rare neuromuscular disorder XLMTM, with 80% efficacy…
Breakthrough CRISPR Therapy Achieves Full Reversal of Rare Muscle Disorder in Landmark Clinical Trial
In a medical milestone, CRISPR gene therapy has fully reversed symptoms of…
